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Your search returned 15 studies. (Get alerts for new studies):Growth and Development Study of MyozymeConditions: Pompe Disease - Glycogen Storage Disease Type II (GSD-II) - Acid Maltase Deficiency Disease4 Locations availableImmune Tolerance Induction StudyConditions: Pompe Disease - Glycogen Storage Disease Type II (GSD-II) - Glycogenesis 2 Acid Maltase Deficiency4 Locations availablePompe Disease RegistryConditions: Glycogen Storage Disease Type II - Pompe Disease1 Location availableSafety Study of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase to Treat Pompe DiseaseConditions: Pompe Disease1 Location availableExtension Study for Patients Who Have Completed BMN 701 StudiesConditions: Pompe Disease2 Locations availablePregnancy and Birth Outcome in Women With Pompe DiseaseConditions: Pompe Disease1 Location availableObservational Study for Children With Pompe Disease Undergoing Immune Modulation TherapiesConditions: Pompe Disease1 Location availablePompe Lactation Sub-RegistryConditions: Glycogen Storage Disease - Pompe Disease1 Location availableSafety/Tolerability/Pharmacokinetic (PK)/Pharmacodynamics (PD) Study of BMN701 in Patients With Late-Onset Pompe DiseaseConditions: Pompe Disease4 Locations availableExploratory Muscle Biopsy Assessment Study in Patients With Late-Onset Pompe Disease Treated With Alglucosidase AlfaConditions: Pompe Disease (Late-Onset) - Glycogen Storage Disease Type II (GSD II) - Glycogenesis 2 Acid Maltase Deficiency7 Locations availablePharmacokinetics of Alglucosidase Alfa in Patients Aged 8-18 Years of AgeConditions: Pompe Disease (Late-Onset) - Glycogen Storage Disease Type II (GSD II) - Glycogenesis 2 - Acid Maltase Deficiency1 Location availableA Study to Evaluate the Efficacy and Safety of Alglucosidase Alfa Produced at the 4000 L Scale for Pompe DiseaseConditions: Pompe Disease47 Locations availablePompe Pregnancy Sub-RegistryConditions: Glycogen Storage Disease Type II (GSD-II) - Pompe Disease (Late-onset) - Glycogenesis 2 Acid Maltase Deficiency1 Location availableDrug-drug Interaction StudyConditions: Pompe Disease8 Locations availableA Noninferiority Study of Alglucosidase Alfa Manufactured at the 160 L and 4000 L Scales in Patients With Infantile-Onset Pompe Disease Who Have NeverConditions: Pompe Disease (Infantile-Onset) - Glycogen Storage Disease Type II (GSD II) - Glycogenosis 2 - Acid Maltase Deficiency1 Location available
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