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Your search returned 16 studies. (Get alerts for new studies):Stem Cell Transplant for HemoglobinopathyConditions: Sickle Cell Disease - Thalassemia - Severe Congenital Neutropenia - Diamond-Blackfan Anemia - Shwachman-Diamond Syndrome1 Location availableRetroviral Vector Mediated Globin Gene Transfer to Correct Sickle Cell Anemia or ThalassemiaConditions: Sickle Cell Anemia - Thalassemia1 Location availableReduced Intensity Conditioning for Umbilical Cord Blood Transplant in Pediatric Patients With Non-Malignant DisordersConditions: Non Malignant Disorders - Immunodeficiencies - Congenital Marrow Failures - Hemoglobinopathies - Inborn Errors of Metabolism - Sickle Cell - Thalassemia - Lysosomal Storage Disease1 Location availableGlutamine Therapy for Hemolysis-Associated Pulmonary HypertensionConditions: Pulmonary Hypertension - Sickle Cell Disease - Thalassemia1 Location availableSafety, Efficacy and Pharmacokinetics of an Oral Iron Chelator Given for a Year to Pediatric Patients With Iron OverloadConditions: Transfusional Iron Overload - Beta-Thalassemia1 Location availableAllo-HCT MUD for Non-malignant Red Blood Cell (RBC) Disorders: Sickle Cell, Thal, and DBA: Reduced Intensity Conditioning, Co-tx MSCsConditions: Sickle Cell Disease - Thalassemia - Diamond-Blackfan Anemia2 Locations availableStem Cell Transplant in Patients With ThalassemiaConditions: Thalassemia1 Location availableGenes Influencing Iron Overload StateConditions: Sickle Cell Disease - Thalassemia - Marrow Aplasia1 Location availableUnrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood CellsConditions: Sickle Cell Disease - Thalassemia - Anemia - Granuloma - Wiskott-Aldrich Syndrome - Chediak Higashi Syndrome - Osteopetrosis - Neutropenia - Thrombocytopenia - Hurler Disease - Niemann-Pick Disease - Fucosidosis1 Location availableIron Balance Study of Deferasirox, Deferoxamine and the Combination of BothConditions: Thalassemia1 Location availableReduced Intensity Transplant Conditioning Regimen for Severe ThalassemiaConditions: Severe Thalassemia9 Locations availableMulti-Center Study of Iron Overload: Pilot and Survey StudyConditions: Sickle Cell Disease - Thalassemia - Diamond-Blackfan Anemia1 Location availableStem Cell Transplant in Sickle Cell Disease and ThalassemiaConditions: Sickle Cell Disease - Beta Thalassemia1 Location availableA Phase III Safety and Efficacy Study of L-Glutamine to Treat Sickle Cell Disease or Sickle βo-thalassemiaConditions: Sickle Cell Anemia - Sickle ß0-Thalassemia28 Locations availableHigh-Tc Susceptometer to Monitor Transfusional Iron OverloadConditions: Transfusional Iron Overload - Thalassemia Major - Sickle Cell Disease - Myelodysplastic Syndromes - Aplastic Anemia1 Location availableStudy of Fludarabine Drug Exposure in Pediatric Bone Marrow TransplantationConditions: Hematologic Malignancies - Nonmalignant Diseases - Immunodeficiencies - Hemoglobinopathies - Genetic Inborn Errors of Metabolism - Fanconi's Anemia, - Thalassemia - Sickle Cell Disease1 Location available
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