Expired Study
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Clinical Trial 16432

Decatur, GA 30033

Study Summary:

The purpose of this study is to find out more about some of the unusual chemicals (called oligosaccharides) that can occur naturally as a result of processes in the body. Researchers want to look at how these chemicals change with time and how they change between different patients with MPSIVA. These unusual chemicals were recently discovered in the urine from patients with MPSIVA. We would like to study these chemicals before a specific enzyme replacement therapy is used. If we understand how these chemicals change, we may be able to use them to monitor this condition in the near future as well as help doctors know whether certain therapies work well in their patients.

Qualified Participants Must:

• Be diagnosed with MPS IVA (Morquio A syndrome)
• Not be receiving enzyme replacement therapy (ERT)

Qualified Participants May Receive:

You and/or your relatives will not be offered payment for being in this study. There is no treatment as part of this study.

Clinical trials are medical research studies designed to test the safety and/or effectiveness of new investigational drugs, devices, or treatments in humans. These studies are conducted worldwide for a range of conditions and illnesses. Learn more about clinical research and participating in a study at About Clinical Trials.